Sponsored Projects

Sponsored Project: Correction of Albinism Mutations By Targeted Genomic Rearrangements

The Vision for Tomorrow Foundation is pleased to be funding a research project by University of Arizona Professor of Pediatrics, Dr. Murray H. Brilliant. The goal of his research is to develop a novel gene therapy approach that is able to direct genomic rearrangements in living organisms. This approach will make it possible to correct a genetic mutation which prevents the cells of the eye from making pigment.

The project draws on cutting-edge research in protein engineering and gene therapy, as well as Dr. Brilliant’s previous work using animal models of albinism (such as mice).

The success of the project is expected to lead to therapeutic interventions for albinism. A secondary benefit would be the development of tools and technology that may impact other areas of human genetic diseases.

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